Rare Genetic Diseases
Focusing on modulating the extremes of amino acid metabolism, we use novel engineered human enzymes to reduce amino acid toxicity in the blood. For patients with rare genetic diseases (like Arginase 1 Deficiency) who currently have limited treatment options, we believe in a better future through enzyme therapy.
Cancer
We’re unlocking the potential of enzyme therapy to deprive certain cancers of the key amino acids they depend on. It’s a well described but not yet broadly applied concept with the potential to transform lives for a variety of diseases associated with abnormal amino acid metabolism.
