Current Clinical Trials
We are conducting a clinical trial to assess the safety and efficacy of our enzyme replacement therapy in patients with Arginase I Deficiency.
- PEACE (Pegzilarginase Effect on Arginase 1 Deficiency Clinical Endpoints): A Randomized, Double-blind, Placebo-controlled Phase 3 Study of the Efficacy and Safety of Pegzilarginase in Children and Adults With Arginase 1 Deficiency – NCT03921541 – Recruiting
- An Open-label, Multicentre Extension Study to Evaluate the Long-Term Safety, Tolerability and Effects of Intravenous Pegzilarginase in Patients With Arginase I Deficiency Who Previously Received Treatment in Study CAEB1102-101A – NCT03378531 – Active, not recruiting
Thank you to the patients, families and physicians who contribute to our collective knowledge and to the potential of future therapies by considering involvement in clinical trials.